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    Rare Disease Analyser – EBStatMax Tool

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    Research and Drug Development

    1. Showing 80 results for:
    2. Research and Drug Development
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    Rare Disease Analyser – EBStatMax Tool

    Published by

    Research and Drug Development

    The ready-to-use version of the EBStatMax tool.

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    A neutral comparison of statistical methods for analyzing longitudinally measured ordinal outcomes in rare diseases

    Published by Wiley

    Research and Drug DevelopmentClinical Trial Design

    peer reviewed journal article on a neutral comparison of statistical methods for longitudinal ordinal outcomes

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    How to Analyze Continuous and Discrete Repeated Measures in Small-Sample Cross-Over Trials?

    Published by Oxford Academic

    Research and Drug DevelopmentClinical Trial Design

    peer reviewed journal article on a neutral comparison of statistical methods for longitudinal count data and binary data

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    Statistical recommendations for count, binary, and ordinal data in rare disease cross-over trials

    Published by Springer

    Clinical Trial DesignResearch and Drug DevelopmentGuidelines

    peer reviewed journal article on statistical recommendations for longitudinal cross-over studies in rare disease research

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    Learning video project overview

    Published by EBStatMax team

    Research and Drug DevelopmentClinical Trial Design

    Learning Video on the EBStatMax Project Overview

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    Learning video statistical recommendations

    Published by EBStatMax team

    GuidelinesResearch and Drug DevelopmentClinical Trial Design

    Learning Video on the EBStatMax Project Overview

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    Learning video educational materials

    Published by EBStatMax team

    Clinical Trial DesignResearch and Drug Development

    Learning Video on educational materials

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    Learning video Rare Disease Analyser

    Published by EBStatMax team

    Patient DataClinical Trial DesignResearch and Drug Development

    Learning Video on the Rare Disease Analyser

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    Rare Disease Analyser GitHub repository

    Published by Konstantin Emil Thiel (EBStatMax)

    Patient DataClinical Trial DesignResearch and Drug Development

    Source code of the Rare Disease Analyser, the webapp that implements statistical methods for rare diseases

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    User Manual for the Rare Disease Analyser

    Published by EBStatMax team

    Research and Drug DevelopmentClinical Trial DesignPatient Data

    detailed instructions on how to use the RDA

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    The Innovation Management Toolbox was originally developed through funding from the EJP RD project, which received funding from the European Union’s Horizon 2020 research and innovation programme under grant agreement No. 825575. The continued development and maintenance of the Toolbox are now supported by the ERDERA partnership, funded under the European Union’s Horizon Europe Research & Innovation programme, grant agreement No. 101156595.
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